iDrugBank

Abetalipoproteinemia

MESHD000012

An autosomal recessive disorder of lipid metabolism. It is caused by mutation of the microsomal triglyceride transfer protein that catalyzes the transport of lipids (TRIGLYCERIDES; CHOLESTEROL ESTERS; PHOSPHOLIPIDS) and is required in the secretion of BETA-LIPOPROTEINS (low density lipoproteins or LDL). Features include defective intestinal lipid absorption, very low serum cholesterol level, and near absent LDL.

Synonyms

  • Bassen-Kornzweig Syndrome
  • Bassen Kornzweig Syndrome
  • Microsomal Triglyceride Transfer Protein Deficiency Disease
  • Bassen-Kornzweig Disease
  • Bassen Kornzweig Disease
  • Microsomal Triglyceride Transfer Protein Deficiency
  • Betalipoprotein Deficiency Disease
  • Betalipoprotein Deficiency Diseases
  • Deficiency Disease, Betalipoprotein
  • Deficiency Diseases, Betalipoprotein
  • Disease, Betalipoprotein Deficiency
  • Diseases, Betalipoprotein Deficiency
  • Acanthocytosis
  • Acanthocytoses

Source last updated 2026-05-24T15:28:24.502Z